Editorial: Genome and transcriptome editing to understand and treat neuromuscular diseases

Frontiers in Genome Editing

Genome Editing

Alyson Fiorillo¹  Christopher Heier¹  Toshifumi Yokota²  Rika Maruyama²  Dongsheng Duan³ 

[1] Center for Genetic Medicine Research, Children’s National Hospital, Washington, DC, United States;Department of Medical Genetics, University of Alberta Faculty of Medicine and Dentistry, Edmonton, AB, Canada;Department of Molecular Microbiology and Immunology, School of Medicine, The University of Missouri, Columbia, MO, United States;

关键词: amyotrophic lateral sclerosis;    5′UTR;    shRNAs;    antisense oligonucleotides;    GNE;    microRNA;    Duchenne muscular dystrophy;    SOD1;   

DOI  :  10.3389/fgeed.2023.1176699

 received in 2023-02-28, accepted in 2023-03-06,  发布年份 2023

来源: Frontiers

【 授权许可】

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Copyright © 2023 Maruyama, Fiorillo, Heier, Duan and Yokota.