Development of a novel PRO instrument for use in familial chylomicronemia syndrome

Journal of Patient-Reported Outcomes

Andrew Hsieh¹  Montserrat Vera-Llonch¹  David Davidson²  Christina Slota³  Sheri Fehnel³  T. Michelle Brown³ 

[1] Ionis Pharmaceuticals, 2855 Gazelle Court, 92010, Carlsbad, CA, USA;NorthShore University HealthSystem, 2151 Waukegan Rd, 60015, Bannockburn, IL, USA;RTI Health Solutions, 3040 East Cornwallis Road, 27709, Research Triangle Park, NC, USA;

关键词: Familial chylomicronemia syndrome;    Patient-reported outcomes;    PRO measure;    FCS Symptoms and Impacts Scale;    Clinical outcome assessment;    COA;   

DOI  :  10.1186/s41687-021-00347-5

来源: Springer

【 授权许可】

CC BY